REVIEW
|
doi:10.20944/preprints202301.0139.v1
Subject:
Medicine And Pharmacology,
Pediatrics, Perinatology And Child Health
Keywords:
eteplirsen; golodirsen; viltolarsen; casimersen; WVE-N531; SRP-5051; DS-5141B; NS-089/NCNP-02; SCAAV9.U7.ACCA; ATL1102
Online: 9 January 2023 (04:18:24 CET)
REVIEW
|
doi:10.20944/preprints202307.1409.v1
Subject:
Biology And Life Sciences,
Life Sciences
Keywords:
spinal and bulbar muscular atrophy; antisense therapy; oligonucleotide; splice switching; mRNA knockdown; androgen receptor; AR45
Online: 20 July 2023 (09:53:18 CEST)