REVIEW
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doi:10.20944/preprints202402.1738.v1
Subject:
Biology And Life Sciences,
Neuroscience And Neurology
Keywords:
Antisense oligonucleotides (ASOs); motor neuron diseases; spinal muscular atrophy; amyotrophic lateral sclerosis; spinal and bulbar muscular atrophy; innovative therapy; nusinersen; tofersen; clinical trals
Online: 1 March 2024 (03:10:14 CET)