REVIEW
|
doi:10.20944/preprints202307.1409.v1
Subject:
Biology And Life Sciences,
Life Sciences
Keywords:
spinal and bulbar muscular atrophy; antisense therapy; oligonucleotide; splice switching; mRNA knockdown; androgen receptor; AR45
Online: 20 July 2023 (09:53:18 CEST)
ARTICLE
|
doi:10.20944/preprints202307.0403.v1
Subject:
Biology And Life Sciences,
Cell And Developmental Biology
Keywords:
Bulbar melanocytes; Hair Follicle (HF); Follicular-Melanin-Unit (FMU); Melanin; C-KIT; MITF; SOX10; Melan A
Online: 6 July 2023 (09:04:00 CEST)
REVIEW
|
doi:10.20944/preprints202402.1738.v1
Subject:
Biology And Life Sciences,
Neuroscience And Neurology
Keywords:
Antisense oligonucleotides (ASOs); motor neuron diseases; spinal muscular atrophy; amyotrophic lateral sclerosis; spinal and bulbar muscular atrophy; innovative therapy; nusinersen; tofersen; clinical trals
Online: 1 March 2024 (03:10:14 CET)