ARTICLE
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doi:10.20944/preprints202302.0033.v1
Subject:
Medicine And Pharmacology,
Pathology And Pathobiology
Keywords:
Neuromuscular disorder; NCALD; SMA; SMN2; Antisense oligonucleotide; Genetic modifier; Therapy; hiPSCs
Online: 2 February 2023 (07:54:05 CET)