REVIEW
|
doi:10.20944/preprints202201.0016.v2
Subject:
Engineering,
Control And Systems Engineering
Keywords:
AI; deep learning; video editing; image editing
Online: 4 February 2022 (13:40:05 CET)
ARTICLE
|
doi:10.20944/preprints202105.0422.v1
Subject:
Medicine And Pharmacology,
Immunology And Allergy
Keywords:
genome editing; CRISPR; Cas9; in vivo editing
Online: 18 May 2021 (11:27:46 CEST)
REVIEW
|
doi:10.20944/preprints202209.0117.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
abiotic stress tolerance; base editing; CRISPR/Cas9; crop production; gene editing; prime editing
Online: 8 September 2022 (03:31:39 CEST)
REVIEW
|
doi:10.20944/preprints202103.0291.v1
Subject:
Biology And Life Sciences,
Anatomy And Physiology
Keywords:
secondary epimutations; repeat associated diseases; genetic editing; epigenetic editing; transcriptional editing; DNA methylation; histone modifications
Online: 10 March 2021 (16:14:10 CET)
REVIEW
|
doi:10.20944/preprints202011.0667.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Plant breeding; Genome editing; Molecular breeding; Prime editing; Base editing; CRISPR Cas; Epigenetics; Speed breeding
Online: 26 November 2020 (11:17:56 CET)
REVIEW
|
doi:10.20944/preprints202312.2257.v1
Subject:
Biology And Life Sciences,
Plant Sciences
Keywords:
Pathogen Derived Resistance; RNA silencing; artificial miRNA; tasiRNA; Epigenetic editing; prime editing; Multiplexing CRISPR/Cas editing
Online: 29 December 2023 (05:55:13 CET)
REVIEW
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
synthetic biology; CRISPR; Cas9; biotechnology; biodesign; nickase; base editing; prime editing; genome editing; ethics; responsible innovation
Online: 1 October 2020 (08:38:22 CEST)
REVIEW
|
doi:10.20944/preprints202212.0184.v1
Subject:
Biology And Life Sciences,
Plant Sciences
Keywords:
CRISPR; genome editing; gene editing; forage grass; abiotic stress; plant
Online: 12 December 2022 (01:38:47 CET)
REVIEW
|
doi:10.20944/preprints202107.0182.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
CRISPR-Cas9; Genome editing; plant editing; bacterial immune system; genetic disease
Online: 8 July 2021 (09:50:22 CEST)
CONCEPT PAPER
|
doi:10.20944/preprints202404.1620.v3
Subject:
Biology And Biotechnology,
Biology And Life Sciences
Keywords:
microglial replacement; adeno-associated viral (AAV) vectors; COURIER; SPIT; base editing; prime editing
Online: 24 May 2024 (11:34:33 CEST)
REVIEW
|
doi:10.20944/preprints202401.1662.v1
Online: 23 January 2024 (07:54:00 CET)
REVIEW
|
doi:10.20944/preprints202312.0905.v1
Subject:
Chemistry And Materials Science,
Medicinal Chemistry
Keywords:
Cas9; Small Molecules; Genome Editing
Online: 12 December 2023 (16:11:02 CET)
REVIEW
|
doi:10.20944/preprints202009.0490.v1
Subject:
Biology And Life Sciences,
Cell And Developmental Biology
Keywords:
base editing; prime editing; ABE; SCD; sickle cell disease; sickle cell anemia; CRISPR; Cas9
Online: 21 September 2020 (04:23:21 CEST)
REVIEW
|
doi:10.20944/preprints202312.1207.v1
Subject:
Biology And Life Sciences,
Animal Science, Veterinary Science And Zoology
Keywords:
Precision gene editing; CRISPR/Cas9; Livestock genetic breeding; Cashmere goat; Editing efficiency; Fixed point integration
Online: 15 December 2023 (16:46:01 CET)
REVIEW
|
doi:10.20944/preprints202307.2018.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
biotechnology; omics; MAS; genome editing; RNAi
Online: 28 July 2023 (11:52:02 CEST)
REVIEW
|
doi:10.20944/preprints202304.0326.v1
Subject:
Biology And Life Sciences,
Animal Science, Veterinary Science And Zoology
Keywords:
Sheep, genome, transcriptome, pangenome, gene editing
Online: 13 April 2023 (14:08:04 CEST)
ARTICLE
|
doi:10.20944/preprints202311.1585.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
prime editing; CRISPR/Cas9; gene editing; gene therapy; RYR1-related diseases; neuromuscular diseases; RYR1 gene; mutations
Online: 24 November 2023 (08:51:01 CET)
REVIEW
|
doi:10.20944/preprints202307.2062.v1
Subject:
Medicine And Pharmacology,
Clinical Medicine
Keywords:
gene editing; gene therapy; FDA; regulatory approval
Online: 31 July 2023 (04:55:07 CEST)
REVIEW
|
doi:10.20944/preprints202111.0084.v1
Subject:
Medicine And Pharmacology,
Neuroscience And Neurology
Keywords:
Parkinson’s disease; gene therapy; mitochondria; genome editing
Online: 3 November 2021 (14:17:16 CET)
REVIEW
|
doi:10.20944/preprints202109.0264.v1
Subject:
Biology And Life Sciences,
Animal Science, Veterinary Science And Zoology
Keywords:
choanoflagellates; multicellularity; animal origins; genome editing; electroporation
Online: 15 September 2021 (14:39:19 CEST)
REVIEW
|
doi:10.20944/preprints202101.0212.v1
Subject:
Medicine And Pharmacology,
Immunology And Allergy
Keywords:
CML; CRISPR/Cas9; BCR/ABL1; genome editing
Online: 12 January 2021 (10:14:46 CET)
REVIEW
Subject:
Business, Economics And Management,
Economics
Keywords:
new plant engineering techniques (NPETs); new breeding techniques (NBTs); genome editing; gene editing; cisgenic; willingness to pay (WTP)
Online: 1 October 2021 (12:55:10 CEST)
REVIEW
|
doi:10.20944/preprints202405.1165.v1
Subject:
Biology And Biotechnology,
Biology And Life Sciences
Keywords:
virus genetic diversity; gene editing; plant disease; biotechnology.
Online: 17 May 2024 (11:43:10 CEST)
ARTICLE
|
doi:10.20944/preprints202405.0728.v1
Subject:
Agricultural Science And Agronomy,
Biology And Life Sciences
Keywords:
Rice; Flowering period; Multiplex Genome Editing; Breed improvement
Online: 12 May 2024 (07:44:38 CEST)
REVIEW
|
doi:10.20944/preprints202401.1948.v2
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
CRISPR-Cas technology; Endonuclease recycling; Genome Editing; Implications
Online: 12 April 2024 (08:41:23 CEST)
REVIEW
|
doi:10.20944/preprints202310.1389.v1
Subject:
Medicine And Pharmacology,
Otolaryngology
Keywords:
genetics; genomics; deafness; inner ear; cochlea; delivery; editing
Online: 23 October 2023 (10:52:29 CEST)
REVIEW
|
doi:10.20944/preprints202309.0786.v1
Subject:
Biology And Life Sciences,
Immunology And Microbiology
Keywords:
herpesvirus; ADAR; RNA editing; miRNA; latency; innate immunity
Online: 13 September 2023 (02:43:06 CEST)
REVIEW
|
doi:10.20944/preprints202309.0168.v1
Subject:
Biology And Life Sciences,
Agricultural Science And Agronomy
Keywords:
abiotic stress; CRISPR/Cas9; genome editing; genome databases
Online: 5 September 2023 (02:36:28 CEST)
ARTICLE
|
doi:10.20944/preprints202307.1967.v1
Subject:
Biology And Life Sciences,
Plant Sciences
Keywords:
kiwifruit; pentatricopeptide repeat protein; pathogens stress; RNA editing
Online: 28 July 2023 (08:05:40 CEST)
ARTICLE
|
doi:10.20944/preprints202109.0362.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
Target-AID; porcine; pig; base editing; CRISPR/Cas
Online: 21 September 2021 (12:34:20 CEST)
REVIEW
|
doi:10.20944/preprints202011.0603.v1
Subject:
Biology And Life Sciences,
Agricultural Science And Agronomy
Keywords:
genome editing, agriculture, crispr, talen, specificity, off-target
Online: 24 November 2020 (08:35:00 CET)
REVIEW
|
doi:10.20944/preprints202404.0435.v1
Subject:
Biology And Life Sciences,
Plant Sciences
Keywords:
CRISPR-Cas system; crop improvement; genome engineering; prime editing
Online: 5 April 2024 (12:50:19 CEST)
ARTICLE
|
doi:10.20944/preprints202403.0370.v1
Subject:
Biology And Life Sciences,
Animal Science, Veterinary Science And Zoology
Keywords:
Ningxiang pigs; miRNA editing; high-throughput sequencing; fat deposition
Online: 7 March 2024 (08:19:34 CET)
REVIEW
|
doi:10.20944/preprints202311.2011.v1
Subject:
Medicine And Pharmacology,
Immunology And Allergy
Keywords:
allogeneic; chimeric antigen receptor; off-the-shelf; gene editing
Online: 1 December 2023 (03:05:54 CET)
ARTICLE
|
doi:10.20944/preprints202306.2128.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
Wheat, Agrobacterium-mediated transformation, Gene editing, CRISPR/Cas9, Epigenetics
Online: 3 July 2023 (11:58:59 CEST)
REVIEW
|
doi:10.20944/preprints202305.1887.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
CRISPR/Cas; TALEN; ZFN; Fruit Plants; Genome Editing Systems
Online: 26 May 2023 (08:09:07 CEST)
ARTICLE
|
doi:10.20944/preprints202112.0501.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
miRNA isoform; isomiR, miRNA editing; lung adenocarcinoma; race-disparities
Online: 31 December 2021 (10:41:04 CET)
ARTICLE
|
doi:10.20944/preprints202112.0117.v1
Subject:
Computer Science And Mathematics,
Artificial Intelligence And Machine Learning
Keywords:
post-editing; machine translation; Portuguese; English; translationese; post-editese
Online: 8 December 2021 (09:43:11 CET)
REVIEW
|
doi:10.20944/preprints202105.0376.v1
Subject:
Medicine And Pharmacology,
Oncology And Oncogenics
Keywords:
Gene Editing; Gene Therapy; Oncology; Comparative Medicine; One Health
Online: 17 May 2021 (09:45:43 CEST)
ARTICLE
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
BE4; CRISPR-Cas9; Tyr; cytosine base editing; mouse model
Online: 30 December 2019 (11:16:30 CET)
REVIEW
|
doi:10.20944/preprints202404.1335.v1
Subject:
Transplantation,
Medicine And Pharmacology
Keywords:
transplantation; donor; recipient; patient survival; graft; Precision medicine; Gene editing
Online: 23 April 2024 (10:48:36 CEST)
ARTICLE
|
doi:10.20944/preprints202201.0211.v1
Subject:
Biology And Life Sciences,
Plant Sciences
Keywords:
microalgae; CRISPR/Cas9; gene editing; spermidine; SPD1; auxotrophy; selectable marker
Online: 14 January 2022 (11:55:22 CET)
REVIEW
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Mollusc; selective breeding; gene editing; disease resistance; transgenesis; CRISPR/Cas9
Online: 15 October 2020 (16:06:27 CEST)
REVIEW
|
doi:10.20944/preprints202007.0578.v1
Subject:
Biology And Life Sciences,
Plant Sciences
Keywords:
CRISPR; CAS9; CAS12a; NHEJ; Base editing; PAM; Temperature Sensitivity; Agriculture
Online: 24 July 2020 (11:43:03 CEST)
ARTICLE
|
doi:10.20944/preprints201811.0159.v1
Subject:
Biology And Life Sciences,
Insect Science
Keywords:
Bombyx mori; BmNPV; antiviral therapeutic; CRISPR/Cas9; multi-gene editing
Online: 7 November 2018 (10:23:52 CET)
REVIEW
|
doi:10.20944/preprints202403.0215.v1
Subject:
Biology And Life Sciences,
Virology
Keywords:
Plant immunity; Tobamovirus; RNA silencing; RNA decay; NLR; Phytohormone; Genome editing
Online: 5 March 2024 (06:30:52 CET)
ARTICLE
|
doi:10.20944/preprints202312.0178.v1
Subject:
Biology And Life Sciences,
Cell And Developmental Biology
Keywords:
myeloid cells; FURIN protease; gene editing; functional assays; genomics; cytokine secretion
Online: 4 December 2023 (10:18:09 CET)
REVIEW
|
doi:10.20944/preprints202309.1000.v1
Subject:
Medicine And Pharmacology,
Medicine And Pharmacology
Keywords:
oligonucleotide therapeutic; triplex-forming oligonucleotide; peptide nucleic acid; antigene; genome editing
Online: 14 September 2023 (11:37:06 CEST)
REVIEW
|
doi:10.20944/preprints202211.0318.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Genome editing 4; C. elegans 5; Genome engineering; CRISPR; CRISPR-Cas
Online: 17 November 2022 (02:22:43 CET)
REVIEW
|
doi:10.20944/preprints202201.0265.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
CRISPR; gene editing; Duchenne muscular dystrophy (DMD); exon skipping; NHEJ; dystrophin
Online: 18 January 2022 (17:30:37 CET)
ARTICLE
|
doi:10.20944/preprints202011.0723.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Fanconi anemia; gene editing; FANCA; head and neck cancer; CRISPR/Cas9
Online: 30 November 2020 (11:55:45 CET)
ARTICLE
|
doi:10.20944/preprints202008.0423.v1
Subject:
Biology And Life Sciences,
Agricultural Science And Agronomy
Keywords:
gene editing; mutagenesis; genetically modified; GMO; crop breeding; RNP; genetic screening
Online: 20 August 2020 (04:34:55 CEST)
REVIEW
|
doi:10.20944/preprints202207.0404.v1
Subject:
Biology And Life Sciences,
Plant Sciences
Keywords:
Abiotic stress; biotic stress; biotechnology; climate change; CRISPR; crop improvement; genome editing
Online: 26 July 2022 (10:44:22 CEST)
REVIEW
|
doi:10.20944/preprints202201.0342.v1
Subject:
Biology And Life Sciences,
Agricultural Science And Agronomy
Keywords:
Anthocyanin biosynthesis; biosafety regulations; colored vegetables; crossbreeding; gene editing; human health; transgenes
Online: 24 January 2022 (10:38:22 CET)
REVIEW
|
doi:10.20944/preprints202106.0363.v1
Subject:
Biology And Life Sciences,
Anatomy And Physiology
Keywords:
Traditional food crops; Climate change; Food security; Omics; Translational genomics; Gene editing
Online: 14 June 2021 (13:02:24 CEST)
ARTICLE
|
doi:10.20944/preprints202105.0333.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
genome editing; CRISPR; protoplast; , targeted mutagenesis; TREX2; construct validation; transi-ent expression
Online: 14 May 2021 (13:44:26 CEST)
REVIEW
|
doi:10.20944/preprints202403.0393.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
DNA; Molecular Choreography; Genetic Information; Epigenetic Modifications; CRISPR-Cas9; DNA Replication; Gene Editing
Online: 8 March 2024 (01:54:59 CET)
ARTICLE
|
doi:10.20944/preprints202312.0701.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
Saccharomyces cerevisiae; genome editing; site-directed mutagenesis; CRISPR/Cas9; high-fidelity Cas9 forms
Online: 12 December 2023 (07:43:14 CET)
ARTICLE
|
doi:10.20944/preprints202305.0072.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
APOBEC3A; carcinogenesis; DNA deamination; DNA mutation, hepatocellular carcinoma; molecular mechanism; RNA editing; tumorigenesis
Online: 2 May 2023 (08:12:34 CEST)
REVIEW
|
doi:10.20944/preprints202211.0169.v1
Subject:
Biology And Life Sciences,
Virology
Keywords:
viroid; resistance; tolerance; RNA silencing; plant hormone; spray-induced gene silencing; genome editing
Online: 9 November 2022 (03:10:00 CET)
ARTICLE
|
doi:10.20944/preprints202110.0332.v1
Subject:
Biology And Life Sciences,
Plant Sciences
Keywords:
iPReditor-CMG; RNA editing site; Mitochondrial genomes; genomic sequence feature; support vector machine
Online: 22 October 2021 (15:11:40 CEST)
ARTICLE
|
doi:10.20944/preprints202109.0051.v1
Subject:
Biology And Life Sciences,
Insect Science
Keywords:
Helicoverpa zea; Bollworm; CRISPR; Cry1A; Bt Toxin; Genome Editing; Knockout; Functional Genomics; Resistance
Online: 3 September 2021 (08:19:44 CEST)
REVIEW
|
doi:10.20944/preprints202102.0255.v1
Subject:
Medicine And Pharmacology,
Immunology And Allergy
Keywords:
A-to-I RNA editing; ADAR; microRNAs; microRNA targeting; detection; quantification; functional characterization
Online: 10 February 2021 (12:33:42 CET)
REVIEW
|
doi:10.20944/preprints202003.0351.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
Conventional method; Clustered Regularly Interspaced Short Palindromic Sequence; Genome editing; RNA Interference; TALEN
Online: 23 March 2020 (10:23:45 CET)
REVIEW
|
doi:10.20944/preprints201808.0089.v1
Subject:
Biology And Life Sciences,
Agricultural Science And Agronomy
Keywords:
firmness; Vaccinium; ripening; cell wall; crispy; quantitative genetics; breeding; molecular markers; genome editing
Online: 5 August 2018 (10:11:33 CEST)
ARTICLE
|
doi:10.20944/preprints202404.0058.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
bioactive carotenoid; diatoxanthin; Phaeodactylum tricornutum; CRISPR/Cas9 gene editing; zeaxanthin epoxidase; commercial production line
Online: 2 April 2024 (12:46:38 CEST)
ARTICLE
|
doi:10.20944/preprints202312.0628.v1
Subject:
Biology And Life Sciences,
Virology
Keywords:
IFITM; Influenza A virus; Human cells; WI-38; Genome editing; CRISPR/Cas9; RNA-seq
Online: 8 December 2023 (12:42:54 CET)
REVIEW
|
doi:10.20944/preprints202212.0231.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
methylerythritol phosphate (MEP) pathway; photosynthesis; isoprenoids; lipids; biofuels; gene editing; CRISPR; riboswitch; riboregulators; nanocompartments
Online: 13 December 2022 (07:22:52 CET)
ARTICLE
|
doi:10.20944/preprints201810.0451.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
CTCF; tumour suppressor gene; haploinsufficiency; zinc finger; CRISPR/Cas9; cancer; endometrial cancer; gene editing
Online: 19 October 2018 (11:29:01 CEST)
ARTICLE
|
doi:10.20944/preprints202402.0310.v1
Subject:
Engineering,
Aerospace Engineering
Keywords:
Planet Gear; Rim Crack; Cepstrum Editing; Liftering; Minimum Entropy Deconvolution (MED); Signal Synchronous Average (SSA)
Online: 6 February 2024 (09:18:17 CET)
REVIEW
|
doi:10.20944/preprints202308.0453.v1
Subject:
Medicine And Pharmacology,
Clinical Medicine
Keywords:
gene editing 1; CRISPR 2; gRNA 3; autoimmune disorders 4; nuclease 5; hereditary disorders 6
Online: 4 August 2023 (19:15:10 CEST)
REVIEW
|
doi:10.20944/preprints202306.0686.v1
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
phosphate homeostasis; transcription factors; phosphate starvation response factors; SPX; proteomics; post-translational; CRISPR; gene editing
Online: 9 June 2023 (08:20:58 CEST)
ARTICLE
|
doi:10.20944/preprints202303.0230.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
alpha-synuclein; ADAR; C. elegans; dopamine; neurodegeneration; Parkinson's disease; RNA editing; xanthine dehydrogenase; ABC transporter
Online: 13 March 2023 (10:34:06 CET)
REVIEW
|
doi:10.20944/preprints202207.0100.v1
Subject:
Biology And Life Sciences,
Virology
Keywords:
omicron; alpha; delta; deltacron; recombination; RNA editing; intra-host variants; tropisms; ox-idative damage; Wuhan
Online: 6 July 2022 (15:27:32 CEST)
REVIEW
|
doi:10.20944/preprints202403.0103.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
DNA; genomics; sequencing; gene regulation; precision medicine; DNA nanotechnology; bioinformatics; CRISPR-Cas9; gene editing; personalized Medicine
Online: 4 March 2024 (09:54:47 CET)
REVIEW
|
doi:10.20944/preprints202402.0255.v2
Subject:
Biology And Life Sciences,
Biology And Biotechnology
Keywords:
new genomic techniques (NGT); genetically engineered organisms; genome editing; risk assessment; unintended effects in NGT plants
Online: 6 February 2024 (13:40:47 CET)
REVIEW
|
doi:10.20944/preprints202402.0085.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
CRISPR-Cas System, Biomedicine, Genome engineering, Gene editing, Human disease, Cancer, Animal models Concerns, Benefits, Applications, Function
Online: 1 February 2024 (14:24:57 CET)
REVIEW
|
doi:10.20944/preprints202307.0504.v1
Subject:
Medicine And Pharmacology,
Medicine And Pharmacology
Keywords:
non-viral vectors; polymeric nanoparticles; human inherited diseases; gene editing; nano delivery system; CRISPR/Cas9; viral vectors
Online: 10 July 2023 (02:54:37 CEST)
REVIEW
|
doi:10.20944/preprints201810.0010.v1
Subject:
Medicine And Pharmacology,
Ophthalmology
Keywords:
Gene therapy, gene editing, CRISPR/Cas9, Cas12a, dual AAV, triple AAV, clinical trials, retina, hereditary retinal dystrophies
Online: 1 October 2018 (13:52:23 CEST)
REVIEW
|
doi:10.20944/preprints202402.1643.v1
Subject:
Environmental And Earth Sciences,
Other
Keywords:
Medicinal plants, long-duration space flight, gene-editing, radiation-induced cardiovascular disease, gut microbiome, microgravity
Online: 28 February 2024 (14:01:24 CET)
REVIEW
Subject:
Engineering,
Other
Keywords:
Bioregenerative life support; closed ecological life support; in-situ resource utilization; lunar industrial ecology; 3D bioprinting; gene editing
Online: 28 June 2021 (15:23:39 CEST)
REVIEW
|
doi:10.20944/preprints202401.1524.v1
Subject:
Medicine And Pharmacology,
Ophthalmology
Keywords:
age-related macular degeneration; AMD; vascular endothelial growth factor; VEGF; anti-VEGF therapy; gene therapy; clinical trials; gene editing
Online: 22 January 2024 (10:11:17 CET)
REVIEW
|
doi:10.20944/preprints201907.0211.v2
Subject:
Medicine And Pharmacology,
Pathology And Pathobiology
Keywords:
HIV-1; CRISPR-Cas9; T-cells; lipid nanoparticles; gut-associated-lymphoid tissue; Co-receptors; Probiotics; GI Tract,; Gene Editing
Online: 13 April 2020 (10:57:52 CEST)
ARTICLE
|
doi:10.20944/preprints202404.1124.v1
Subject:
Chemistry And Materials Science,
Nanotechnology
Keywords:
exosomes; proton sponge; RNA; CRISPR/Cas; small molecules; cancer; gene editing; vaccines; biological barriers; nanoparticle-tracking assay; dynamic light scattering
Online: 17 April 2024 (08:40:29 CEST)
CONCEPT PAPER
|
doi:10.20944/preprints202009.0723.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Glycogen Storage Disease Type 1a, Glucose-6-phosphatase Catalytic Subunit (G6PC), Glucose-6-phosphatase (G6Pase), prime editing, mRNA delivery, CRISPR
Online: 30 September 2020 (08:05:17 CEST)
ARTICLE
|
doi:10.20944/preprints202002.0281.v1
Subject:
Medicine And Pharmacology,
Oncology And Oncogenics
Keywords:
matrix metalloproteinase (MMP); moonlighting metalloproteinase; extracellular vesicles; oncosome; genome editing; cell communication network factor 2 (CCN2/CTGF); transcription factor; cancer
Online: 19 February 2020 (11:52:42 CET)
REVIEW
|
doi:10.20944/preprints202201.0073.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Messenger RNA • Hospital-based mRNA therapeutics • circular mRNA • self-amplifying mRNA • RNA-based CAR T-cell • RNA-based gene-editing tools
Online: 6 January 2022 (11:20:59 CET)
REVIEW
|
doi:10.20944/preprints202405.2001.v1
Subject:
Plant Sciences,
Biology And Life Sciences
Keywords:
mosaic-virus; novel viruses; pathogen-derived resistance; RNAi; artificial microRNA; plant gene editing; NB-LRR protein; nanoparticle RNA delivery; plant disease; crop protection
Online: 30 May 2024 (10:51:19 CEST)
REVIEW
|
doi:10.20944/preprints202403.0435.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
3D DNA Structures; Genome Editing (CRISPR-Cas); Genomic Regulation; Genetic Disorders; Computational Genomics; Non-coding RNA Interactions; Ethical, Legal, and Social Implications (ELSI)
Online: 7 March 2024 (12:01:10 CET)
REVIEW
|
doi:10.20944/preprints202104.0484.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
RNA world theory; Viral RNA; Genome stability; Viral evolution; Mutational signatures; RNA dependent RNA polymerase, RdRp; RNA recombination; RNA damage; Hypermutation; APOBEC; ADAR; RNA editing; SARS-CoV-2; rubella virus
Online: 19 April 2021 (13:22:01 CEST)
REVIEW
|
doi:10.20944/preprints201912.0385.v1
Subject:
Medicine And Pharmacology,
Cardiac And Cardiovascular Systems
Keywords:
dilated cardiomyopathy (DCM); hypertrophic cardiomyopathy (HCM); restrictive cardiomyopathy (RCM); arrhythmogenic right ventricular cardiomyopathy (ARVC); left ventricular non-compaction cardiomyopathy (LVNC); Duchenne muscular dystrophy; dystrophin; genome editing; CRISPR/Cas9; Cpf1 (Cas12a)
Online: 29 December 2019 (13:41:48 CET)
REVIEW
|
doi:10.20944/preprints201811.0018.v1
Subject:
Biology And Life Sciences,
Biochemistry And Molecular Biology
Keywords:
Duchenne muscular dystrophy (DMD); CRISPR/Cas9; exon skipping therapy; gene editing; human induced pluripotent stem cells (hiPSCs); immortalized patient muscle cells; mdx mice; humanized dystrophic mouse models; deltaE50-MD dog model
Online: 2 November 2018 (05:14:23 CET)