ARTICLE
|
doi:10.20944/preprints202306.2000.v1
Subject:
Biology And Life Sciences,
Life Sciences
Keywords:
Gene therapy; AAV; dual vector; DMD; dystrophin; homologous recombination; concatemerization
Online: 29 June 2023 (02:06:05 CEST)
ARTICLE
|
doi:10.20944/preprints202205.0020.v1
Subject:
Biology And Life Sciences,
Anatomy And Physiology
Keywords:
limb girdle muscular dystrophies; induced pluripotent stem cells; skeletal muscle cells; pathological modeling
Online: 5 May 2022 (03:44:03 CEST)