ARTICLE
|
doi:10.20944/preprints202405.1298.v1
Subject:
Clinical Medicine,
Medicine And Pharmacology
Keywords:
spinal muscular atrophy; nusinersen; responder; treatment response; patient perception
Online: 20 May 2024 (14:55:31 CEST)
ARTICLE
|
doi:10.20944/preprints202404.1315.v1
Subject:
Neuroscience And Neurology,
Medicine And Pharmacology
Keywords:
spinal muscular atrophy; neuromuscular disease; nusinersen; antisense oligonucleotide; pediatrics
Online: 19 April 2024 (08:05:23 CEST)
ARTICLE
|
doi:10.20944/preprints202311.1564.v1
Subject:
Medicine And Pharmacology,
Neuroscience And Neurology
Keywords:
effectiveness; nusinersen; real-world data; risdiplam; spinal muscular atrophy
Online: 26 November 2023 (05:27:25 CET)
ARTICLE
|
doi:10.20944/preprints202404.1164.v1
Subject:
Neuroscience And Neurology,
Biology And Life Sciences
Keywords:
spinal muscular atrophy; spinal cord stimulation; physical therapy; nusinersen; risdiplam; onasemnogene abeparvovec
Online: 17 April 2024 (13:30:10 CEST)
REVIEW
|
doi:10.20944/preprints202402.1738.v1
Subject:
Biology And Life Sciences,
Neuroscience And Neurology
Keywords:
Antisense oligonucleotides (ASOs); motor neuron diseases; spinal muscular atrophy; amyotrophic lateral sclerosis; spinal and bulbar muscular atrophy; innovative therapy; nusinersen; tofersen; clinical trals
Online: 1 March 2024 (03:10:14 CET)